Hope for Haploinsufficiency Diseases
The Crux,
Genetic conditions like Dravet syndrome, which causes severe childhood epilepsy, are hard to tackle with traditional gene…
Genetic conditions like Dravet syndrome, which causes severe childhood epilepsy, are hard to tackle with traditional gene…
Multi-site phase 1/2a clinical study works to assess safety, dosage of promising drug to treat Dravet syndrome.
Multi-site phase 1/2a clinical study works to assess safety, dosage of promising drug to treat Dravet syndrome.
Development is first step to helping children with the rare epilepsy syndrome.