These Rare Genetic Diseases Are Finally Getting Attention From Drug Companies
Inverse,
The seizures started when Samantha Gundel was just four months old. By her first birthday, she was taking a cocktail of three…
The seizures started when Samantha Gundel was just four months old. By her first birthday, she was taking a cocktail of three…
The seizures started when Samantha Gundel was just four months old. By her first birthday, she was taking a cocktail of three…
This article originally appeared in Knowable Magazine. The seizures started when Samantha Gundel was just four months old.
The seizures started when Samantha Gundel was just four months old. By her first birthday, she was taking a cocktail of three…
Better outcomes: Boosting expression of a sodium channel in a mouse model of Dravet syndrome lowers a mouse's chances of having…
Antisense oligonucleotides increase Scn1a expression and reduce seizures and SUDEP incidence in a mouse model of Dravet…
In a development that may finally offer hope to children with Dravet syndrome and their parents, a new promising…
Data published today in the journal Science Translational Medicine also showed that STK-001 achieved target engagement…
STK-001 has the potential to be the first disease-modifying therapy to address the genetic cause of Dravet syndrome A Phase 1/2a…
BEDFORD, Mass.--(Business Wire)--Stoke Therapeutics, Inc., (Nasdaq: STOK), a biotechnology company pioneering a new way to…
STK-001 has the potential to be the first disease-modifying therapy to address the genetic cause of Dravet syndrome A Phase 1/2a…
Stoke Therapeutics, Inc., (Nasdaq: STOK), a biotechnology company pioneering a new way to treat the underlying cause of genetic…
Illustration for Stoke's proprietary TANGO platform and ASOs. Credit: Provided with permission from Stoke Therapeutics In a…
STK-001 has the potential to be the first disease-modifying therapy to address the genetic cause of Dravet syndrome A Phase 1/2a…
STK-001 has the potential to be the first disease-modifying therapy to address the genetic cause of Dravet syndrome A Phase 1/2a…
In a development that may finally offer hope to children with Dravet syndrome and their parents, a promising investigational…